With 200 experts, Genethon is pursuing its mission to bring life-changing gene therapy products to patients suffering from rare genetic diseases
Joined May 2015
- Tweets 1,313
- Following 207
- Followers 1,055
- Likes 1,348
470 Photos and videos
May 29
Proud to see our teams recognized internationally! Congrats to Djunda Peltier, finalist for the #CommunicationAward
@UFMyology
Her project: a new preclinical model AI tool to better understand and treat calpainopathy.
👉 Like & support her on X:
x.com/ufmyology/status/20596…
Announcing the 4 finalist for the New Directions Conference Communication Award (in no particular order)! Vote for your favorite video and the trainee with the most likes wins! @MYOTWlTTER
Finalist #2 of 4: Djunda Peltier
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May 29
Fiers de voir nos équipes reconnues à l’international !
Bravo Ă notre collaboratrice Djunda Peltier, finaliste du #CommunicationAward @UFMyology
👉 Soutenez son projet en likant sur X : x.com/ufmyology/status/20596…
Announcing the 4 finalist for the New Directions Conference Communication Award (in no particular order)! Vote for your favorite video and the trainee with the most likes wins! @MYOTWlTTER
Finalist #2 of 4: Djunda Peltier
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May 21
📢[COMMUNIQUE DE PRESSE]
@GenethonFr Ă— @AmpersandBio
Un partenariat exclusif pour concevoir des vecteurs AAV à très haute spécificité tissulaire, afin de renforcer la sécurité et l’efficacité des thérapies géniques.
👉urlr.me/AhbdXc
#GeneTherapy #AAV #Innovation
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May 21
📢[PRESS RELEASE]
@GenethonFr Ă— @AmpersandBio
An exclusive partnership to engineer AAV vectors with very high tissue specificity, aiming to enhance the safety and efficacy of gene therapies.
👉 urlr.me/9B3dMJ
#GeneTherapy #AAV #Innovation
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May 15
[#ASGCT2026] – Oral presentations
đź“ŚJoin us for @GenethonFr 's last talks at ASGCT 2026 with:
GĂ©rald Perret, Giuseppe Ronzitti and Paola Galbiati
Advancing clinical gene therapy for rare diseases.
@ASGCTherapy
#GeneTherapy #ClinicalTrials
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May 14
[#ASGCT2026] - Poster session
🤝👨‍🎓 👩‍🎓Meet Genethon scientists presenting:
Estelle Creoff - Poster [ASGCT353]
Adrian Westhaus - Poster [ASGCT1167]
Isabelle Richard - Poster [ASGCT1489]
Youssef Krimi Benchekroun - Poster [ASGCT1891]
Rim Harb - Poster [ASGCT2476]
@ASGCTherapy
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May 14
[#ASGCT2026] – Oral presentation today,
Isabelle Richard, PhD will share expert insights on:
🧬 Challenges and solutions in the development of gene therapy for muscular dystrophies
A key session not to miss.
@ASGCTherapy
#GeneTherapy #MuscularDystrophy #DMD
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May 13
🤝👨‍🎓 👩‍🎓[#ASGCT2026] - Poster session
Meet our teams, discover @GenethonFr's work on genome editing, safety and preclinical models:
Lydie Debaize - Poster [ASGCT1193]
JĂ©rĂ´me Denard - Poster [ASGCT1220]
Badih Salman - Poster [ASGCT870]
@ASGCTherapy
#geneediting #genetherapy
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May 13
[#ASGCT2026] – Oral presentations today
📌Don’t miss oral presentations with Youssef Krimi Benchekroun, Louisa Jauze, Dr. Barry Byrne and Giulia Scalisi.
@ASGCTherapy
#GeneTherapy #RareDiseases
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May 12
[#ASGCT2026] – Poster sessions
📌🤝Explore @GenethonFr's research in gene therapy and genome editing:
Estelle Creoff - Poster [ASGCT355]
Philippe Veron - Poster [ASGCT1186]
Alexandra Tachtsidi - Poster [ASGCT1368]
Rim Harb - Poster [ASGCT1830]
Marion Derome - Poster [ASGCT1163]
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May 11
📢 The 29th Annual #ASGCT2026 Congress kicks off today 11, in Boston, MA! @GenethonFr will present 21 scientific contributions:
- 8 oral presentations
- 13 posters!
urlr.me/FYrAy4
Looking forward to sharing our latest advances in gene therapy!
#GeneTherapy
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🔬 Evaluating a single treatment across multiple diseases that share a common biological mechanism: a promising “basket” clinical trial approach to accelerate therapeutic innovation.
👉urls.fr/yjE3ki
@Telethon_France @Inst_Myologie @IStemFrance
#ClinicalTrials
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🔬 Évaluer un même traitement dans plusieurs maladies partageant un mécanisme biologique commun: une approche prometteuse des essais cliniques "basket" pour accélérer l’innovation thérapeutique.
👉urlr.me/4eAqpC
@Telethon_France @Inst_Myologie @IStemFrance
# essais
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#ASGCT2026 | Genethon at @ASGCTherapy
Efficacy data from 3 gene therapy trials: pivotal GNT0004 (Duchenne), first clinical results of ATA200 (LGMD R5), and first‑in‑patient proof that imlifidase can overcome pre‑existing AAV immunity.
8 talks, 13 posters.
urlr.me/t9qXkJ
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Apr 28
⏰ Good morning fellow #CGMED26 attendees! Day 1 of the conference is underway.
Don’t miss @GenethonFr's activities presentation by Imen Mestiri, PhD, Business Development Lead, April 29th at 3:45 pm.
#GeneTherapy #RareDiseases #BusinessDevelopment #Genother
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New study in Molecular Therapy: @GenethonFr uses #CRISPRCas9 to boost utrophin expression in #Duchenne muscular dystrophy. A mutation‑independent genome editing strategy with promising preclinical benefits.
👉urlr.me/GRYk8Q
#GeneTherapy #GenomeEditing #DMD
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Nouvelle étude dans Molecular Therapy : @GenethonFr utilise l’#éditiondugénome #CRISPRCas9 pour augmenter l’expression de l’utrophine dans la myopathie de #Duchenne. Une stratégie indépendante des mutations, prometteuse en préclinique.
👉urlr.me/U3faPe
#DMD
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GENETHON France retweeted
🎉 100 548 314 € collectés pour le Téléthon 2025 !
Grâce à vous : donateurs, bénévoles, familles, partenaires, chercheurs, grâce à @jesuissanta999, aux artistes, animateurs et aux équipes de @Francetele, cette collecte est EXCEPTIONNELLE !
MERCI đź’›
👉 afm-telethon.fr/fr/actualite…
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Mar 16
@GenethonFr at #SFTCG2026: 4 talks & 8 posters at @ICMParis advancing safe, effective gene therapies. AAV, CRISPR, new preclinical models, immune tolerance, rAAV manufacturing… Meet our teams!
đź“„ Full program: sftcg.fr/event-programme
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Mar 16
@GenethonFr au #SFTCG2026 : 4 talks & 8 posters au @ICMParis pour faire avancer des thérapies géniques sûres et efficaces. AAV, CRISPR, nouveaux modèles précliniques, tolérance immunitaire, production de rAAV… Rencontrez nos équipes !
Programme: sftcg.fr/event-programme
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