gene therapy, genome editing, lentiviral vectors, sickle cell disease, beta-thalassemia, red blood cell, hematopoietic stem cell
Joined May 2022
- Tweets 177
- Following 582
- Followers 460
- Likes 280
49 Photos and videos
Apr 10
Base editing cures beta-thalassemia, happy to have participated to this work!
Nature research paper: Clinical application of base editing for treating β-thalassaemia
go.nature.com/4viSIdA
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Nature research paper: Clinical application of base editing for treating β-thalassaemia
go.nature.com/4viSIdA
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Miccio lab retweeted
📣Register now for the third webinar of the program “EDITSCD & ERN-EuroBloodNet: Focus on Genetic Therapy for People Living with Sickle Cell Disease.”
Join us to better understand how innovative therapies are moving from lab to clinic!
Register now: eurobloodnet.eu/education-2/…
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Miccio lab retweeted
26 Nov 2025
And here it is our last work on Base editing of β0-thalassemia mutations with a nice online cover by Science Translational Medicine!
Thank you to @LabMiccio @Inserm @Imagine Institute and to all our collaborators @marioamendola1
science.org/toc/stm/17/826
26 Nov 2025
This week's issue of #ScienceTranslationalMedicine has arrived!
A transcriptional signature could inform smarter antibiotic use in newborns with sepsis, an approved medication boosts anti-malaria immunity in volunteers, and more. scim.ag/483bUCz
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Miccio lab retweeted
26 Nov 2025
This week's issue of #ScienceTranslationalMedicine has arrived!
A transcriptional signature could inform smarter antibiotic use in newborns with sepsis, an approved medication boosts anti-malaria immunity in volunteers, and more. scim.ag/483bUCz
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6 Nov 2025
It was amazing to host so many brilliant researchers — along with passionate young scientists — in Sorrento, Italy, for the EMBO Workshop “CRISPR-Cas: From Biology to Therapeutic Applications.#EMBOCRISPRcas
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6 Nov 2025
We had fantastic science, a great atmosphere, lively discussions, and plenty of fun, sightseeing, and delicious food!
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6 Nov 2025
A huge thank-you to Guillermo Montoya (@g1_guillermo), Marcello Maresca, Angelo Lombardo, and Toni Cathomen for sharing this adventure as co-organizers — and to all the speakers, presenters and sponsors for making it all possible!
See you in 2025! 🎉
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3 Oct 2025
Congratulations to Letizia Fontana discussing epigenome editing at teh ASCAT conference in London! @ascatconference
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27 Sep 2025
An exciting year for our lab, epigenome , prime editing and now the elegant work by led by Letizia Fontana and Panagiotis Antoniou on multiplex base editing:
cell.com/cell-reports-medici…
Thanks also to Oriana Romano and @marioamendola1 Mario Amendola for the great collaboration!
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9 Sep 2025
Epigenetic editing: a promising alternative to genome editing for treating sickle cell disease and beta-thalassemia
institutimagine.org/en/epige…
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30 Aug 2025
Happy to share our recent work led by @MeganeBrusson in our lab and just published in Blood describing a prime editing strategy to reactivate fetal hemoglobin for sickle cell disease
ashpublications.org/blood/ar…
Congrats to Megane, all the lab members and our collaborators!
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18 Aug 2025
Thérapie génique et drépanocytose : lancement d’une une série de webinaires internationaux pour le grand public
institutimagine.org/fr/thera…
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Miccio lab retweeted
1 Aug 2025
With boost to NIH budget, Senate panel rejects Trump’s plan to slash agency | Science | AAAS science.org/content/article/…
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10 Jul 2025
Happy to share our work published today on Nucleic Acid Research @NAR_Open :
"Dissecting the epigenetic regulation of the fetal hemoglobin genes to unravel a novel therapeutic approach for β-hemoglobinopathies"
academic.oup.com/nar/article…
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30 May 2025
We're thrilled to be organizing a CRISPR-Cas9 workshop in the beautiful city of Sorrento, featuring renowned scientists from around the globe!
meetings.embo.org/event/25-c…
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29 Jun 2025
There's still time to register for the CRISPR-Cas9 workshop - registration has been extended. Participate to the second CRISPR-Cas9 workshop in the beautiful city of Sorrento, featuring renowned scientists from around the globe! meetings.embo.org/event/25-c…
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