Genetic medicines company harnessing Protein Splicing to develop the next-gen of gene therapies. Based on technology developed in the Muir Lab at @Princeton.
Joined February 2018
- Tweets 202
- Following 56
- Followers 327
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Photos and videos
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17 Jun 2025
SpliceBio takes over Times Square! đź—˝
Proud to see our $135M Series B milestone spotlighted on the iconic @Nasdaq Tower.
Huge thanks to our team & investors powering the next wave of genetic medicines! đź’ˇ
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Jun 9
Last week, our team came together for a retreat filled with reflection, connection, and plenty of laughs! Experiences like these reinforce something we believe deeply: investing in our people is essential to building a strong culture and advancing our mission.
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May 20
#Stargardt disease is caused by mutations in ABCA4Â - a gene too large for traditional gene therapy. We're advancing protein splicing to enable large-gene delivery and address the root cause of a disease with no approved treatments.
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May 18
Great time at #ARVO2026 & #ASGCT2026! We were proud to share progress on our clinical program SB-007 for #Stargardt disease and engage in conversations with the broader #genetherapy community. Thank you to everyone who connected. We’re energized by the momentum!
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May 7
#Stargardt disease has no approved treatments. This #HealthyVisionMonth, we’re raising awareness of inherited retinal diseases. At SpliceBio, we’re working to advance genetic medicines using protein splicing to address diseases caused by mutations in large genes.
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May 4
We’re heading to #ASGCT2026 next week! Looking forward to connecting with the community, sharing insights, and contributing to the conversation around #genetherapy at the @ASGCTherapy Annual Meeting. See you there!
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May 1
Great science starts with great people. Today, we celebrate the SpliceBio team whose passion and collaboration power our work in genetic medicines. Thank you for all you do. Happy #InternationalWorkersDay!
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Apr 23
Feliç #SantJordi i #WorldBookDay 🌹📖Avui celebrem una tradició catalana de llibres, roses i històries amb el nostre equip a Barcelona. Un dia per celebrar l’amor i la cultura, amb roses per a tothom!
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Apr 23
Happy #SantJordi and #WorldBookDay 🌹📖
Today, we’re celebrating a Catalan tradition of books, roses and storytelling with our team in Barcelona. Here’s to a day of love and culture, with roses for all!
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Apr 22
Our CMO Aniz Girach will present at the Annual Retinal Therapeutics Innovation Summit in Denver, co-hosted by @FightBlindness and @CaseyEye. He’ll share the progress of our clinical program SB-007, a third-generation intein-based dual AAV in development for Stargardt disease.
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Apr 8
Our co-founder and CEO sat down with @CheckRare to discuss SB-007, our investigational dual-AAV gene therapy for #Stargardt disease, and how it is designed to enable delivery of the full-length ABCA4 protein.
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Mar 8
Our work in genetic medicines is guided by shared values and scientific excellence. We’re grateful to the women at SpliceBio and to those everywhere whose work helps translate discovery into transformative therapies for patients.
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Mar 2
We’re ready for an active week ahead engaging with the #biotech community! Logistics below. We look forward to sharing our progress and connecting with partners.
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Feb 28
For #RareDiseaseDay, we came together to name our newest plush teammate, “Tira,” inspired by a zebra in Kenya born with a rare genetic condition that altered her stripe pattern.🦓Tira is a reminder of why we do this work and who we do it for.
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Feb 11
We have a fierce appreciation for women in STEM! On International Day of Women and Girls in Science, we recognize all of the incredible women at SpliceBio who are transforming the future of genetic medicines and are paving the way for future generations. #WomeninSTEM
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Feb 5
#Stargardt disease is a condition that leads to central vision loss & blindness. Caused by biallelic mutations in the ABCA4 gene, it remains a significant unmet need with no approved treatments. This #LowVisionAwarenessMonth, learn how SB-007 targets the underlying genetic cause.
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Feb 5
Listen to the full episode on The BioHub Podcast.⬇️
Spotify: lnkd.in/e-6YHEBk
Apple: lnkd.in/eyt85Zpx
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Jan 8
We are pleased to announce that the first patient has been dosed in the Part B dose expansion portion of our Phase 1/2 ASTRA clinical trial of SB-007, a dual adeno-associated viral vector gene therapy for the treatment of #Stargardt disease.
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