A major milestone for the Primary Immunodeficiency community: the FDA approval of Rocket Pharmaceuticals' KRESLADI™, marking an important advancement for children living with severe Leukocyte Adhesion Deficiency-I (LAD-I).
This innovative gene therapy represents meaningful progress toward addressing the underlying cause of disease — offering new hope for improved outcomes and quality of life.
We’re also proud to share that Vanessa Tenembaum, CEO of the Jeffrey Modell Foundation, was featured in the announcement, noting: “The approval of KRESLADI represents a significant development for individuals affected by severe LAD-I and the broader primary immunodeficiency community.”
At JMF, we remain committed to advancing research, early diagnosis, and access to life-changing treatments for patients worldwide.
👩💻 Read the full press release here: bit.ly/4va2Fdq
#PrimaryImmunodeficiency #GeneTherapy #LADI #MedicalInnovation #FDApproval #Immunology #PatientAdvocacy #GlobalHealth #JeffreyModellFoundation
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4 Sep 2025
We’re thrilled to announce FDA approval for the Globe® Pulsed Field System, our groundbreaking solution for treating atrial fibrillation.
Welcome to the future of integrated mapping and ablation.
bit.ly/4g0aOtq
#FDApproval #EPeeps x.com/KardiumInc/status/1963…
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26 Oct 2023
#BREAKING: The @US_FDA has approved @Santhera's investigational agent #vamorolone, marketed as Agamree, for the treatment of patients with #DMD. @CatalystForRare will market the agent in North America. #FDApproval #DMDtreatment #FDAnews
Read now:
neurologylive.com/view/fda-a…
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An experimental drug for #Alzheimers showed promise in slowing declines in thinking and #memoryskills when given early in the course of the disease.
alzinfo.org/articles/treatme…
#AlzheimersResearch #BrainHealth #Donanemab #Leqembi #MonoclonalAntibody #BetaAmyloid #FDApproval
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27 Jan 2022
A lot of people are not getting vaxed because it hasn't been tested long enough. Y'all keep making it political:for us it's NOT. I was in R&D for 10 yrs. The issue of testing any drug for just 1 yr & then MANDATING everyone take this exp'mental drug. FDApproval takes 3-5 yrs MIN.
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4 Aug 2021
PharmaTher Granted FDA Orphan Drug Designation For Ketamine To Treat ALS youtu.be/OjTMr8FoNU8 via @YouTube $phrm $phrrf @Pharmather_Inc @RICHTVLIVE @richpickdaily #pharmather #richtvlive #news #business #fda #investing #pennystocks #rich #richtv #education #als #fdapproval #fy
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15 Jan 2021
In the urgent context of medical cures, three-week approval cycle wasn’t sustainable.
Implementing new digital policy procedures that take place “where the work happens” reduced approval cycles from 21-days to just three.
Via @kpodnar 👇
#fdapproval
simplea.com/Articles/improvi…
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7 Dec 2020
New SECRET Penny Stock: Vivos Inc. (OTCQB: RDGL) youtu.be/0eDALhl6fY8 via @YouTube $rdgl #vivosinc #richtvlive #richtv #rich #news #radiogel #breakingnews #pennystocks #money #investing #win #business #finance #gainers #pharma #fda #fdapproval #stockmarket #stockwatch #tips
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4 Dec 2020
In the urgent context of medical cures, three-week approval cycle wasn’t sustainable.
Implementing new digital policy procedures that take place “where the work happens” reduced approval cycles from 21-days to just three.
Via @kpodnar 👇
#fdapproval
simplea.com/Articles/improvi…
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19 Aug 2020
The @US_FDA granted accelerated approval to #Blenrep @GSKUS for adults with relapsed or refractory multiple myeloma.
pharmacypracticenews.com/FDA… @SagarLonialMD @WinshipAtEmory #FDA #fdapproval #myeloma
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8 Aug 2020
The @US_FDA approved a smartphone app that links @AbbottNews #neuromodulation devices to a variety of @Apple products. painmedicinenews.com/Online-… @UToledo @BoettigerKeith #chronicpain #fda #fdapproval
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