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BluePrint Orphan @BluePrintOrphan

Proven excellence in #orphandrug data analytics, forecasting, ​and market access strategy with a special focus in #RareDiseases *retweets/likes ≠ endorsements*

Joined August 2016
  • Tweets 405
  • Following 1,456
  • Followers 270
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BluePrint Orphan@BluePrintOrphan
20 May 2020
Have you been wondering how #COVID19 will affect #orphandrug development? Check out our latest blog post about the pandemic’s impact on the #raredisease sector blueprintorphan.com/developm…
Highlighting our Patient Subtyping capabilities this month. Want to know more? Contact our team today! #raredisease #orphandrug
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Curious about #raredisease treatment development progress in 2020? Check out some of this year's drug approvals! pharmaceutical-technology.co…
Great to see everyone on screen at day 1 of Inborn Errors of Metabolism today! Looking forward to more discussion tomorrow #RareDiseases inborn-errors.com/
Interesting read on how machine learning can be used to help fight #rarediseases pharmalive.com/machine-learn…
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BluePrint Orphan retweeted
National Organization for Rare Disorders (NORD)
@RareDiseases
27 Jul 2020
The #NORDSummit will bring #raredisease leaders & stakeholders together to provide new approaches & fresh perspectives on #publicpolicy, clinical trials, access to #diagnostic testing & pharmaceutical innovation. Register or apply for a scholarship: bit.ly/2WJ7ziE
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Interesting article highlighting the inherent challenges of #orphandrug research and development - our team is here to help! euractiv.com/section/health-…
BluePrint Orphan retweeted
Allucent@Allucent_CRO
3 Jul 2020
Join our experts for a free webinar: The Value of Orphan Drug Designation in your Drug Development Program ow.ly/9KBx50AmOra #OrphanDrug #RareDisease #ClinicalDevelopment #Regulatory #FreeWebinar #ClinialTrials #ClinicalStudies #Innovation Cato Research
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BluePrint Orphan retweeted
National Organization for Rare Disorders (NORD)
@RareDiseases
9 Jul 2020
With the #DISORDER: The #RareDisease Film Festival postponed by the pandemic, the Rare Outreach Coalition decided to start its own streaming channel and bring their content right into your home! Read more: bwnews.pr/2Obbpww

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Thanks to these four families and @nytimes for profiling what life with #raredisease is really like - #orphandrugs and treatments are so important nytimes.com/2020/07/07/healt…

‘It Will Consume Your Life’: 4 Families Take On Rare Diseases (Published 2020)

Confronted by illnesses that most scientists overlook, these families had to work out their own approaches to find treatments.

nytimes.com
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Congrats to #IsaPharmaceuticals for receiving @US_FDA #OrphanDrug Designation for ISA101b in HPV16-positive cervical cancer prnewswire.com/news-releases…

ISA Pharmaceuticals Receives US Orphan-Drug Designation for ISA101b in HPV16-positive Cervical...

/PRNewswire/ -- ISA Pharmaceuticals B.V., a clinical-stage company dedicated to developing rationally designed immunotherapeutics for oncology and infectious...

prnewswire.com
BluePrint Orphan retweeted
RDLA@RareAdvocates
29 Jun 2020
LAST CALL to register for #RareAcrossAmerica Check out this article from @healourskin where Shannon von Felden, #RDLA program director, shares everything you need to know about this unique event. issuu.com/healours…/docs/ippf-100-spring-20-issuu/26

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Interesting article on the discovery of novel genetic causes of #rarediseases healtheuropa.eu/genome-seque…
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BluePrint Orphan retweeted
National Organization for Rare Disorders (NORD)
@RareDiseases
23 Jun 2020
Join #NORD, @CPathInstitute, @US_FDA and @TakedaPharma tomorrow, June 24 at 2:00 PM ET for “Shortening the Timeline for Developing New Treatments – How the Rare Disease Cures Accelerator–Data and Analytics Platform Can Help.” Register: bit.ly/2Bxd10k #RDCADAP #webinar
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Excited to see new funding opportunities for #raredisease research 🎉
National Organization for Rare Disorders (NORD)
@RareDiseases
22 Jun 2020
The National Organization for Rare Disorders (NORD) is pleased to announce new funding opportunities through the Jayne Holtzer #RareDisease #Research Grants Program. Submission of proposals are due by August 25. Read more: bit.ly/2ANmLDO
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Congrats to #ProtagonistTherapeutics on receiving #OrphanDrug Designation for hepcidin mimetic PTG-300
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The @US_FDA has announced that #raredisease patients and #orphandrugs remain priorities during #COVID19 fda.gov/news-events/fda-voic…
Check out this fascinating development in #raredisease diagnostic technology for childhood genetic conditions sciencetimes.com/articles/25…

Childhood Rare Diseases Now Easily Detectable Through 3d Facial Scanning

Diagnosing rare childhood diseases has since then been a hardship for physicians as it usually takes years of tests before a definite diagnosis becomes apparent. Scientists now have come up with a...

sciencetimes.com
Thanks to Dr. @DavidFajgenbaum for sharing your perspective on how #raredisease and #orphandrug research may apply to #COVID19 phillyvoice.com/covid-19-tre…

Rare disease researcher offers unique perspective on search for COVID-19 treatment

Repurposed drug keeps Penn Medicine doctor's rare illness at bay

phillyvoice.com
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Today until July 31, the @US_FDA is seeking comments and feedback from patients, health professionals, and others in the #raredisease community to establish a clinical trials network federalregister.gov/document…

Rare Disease Clinical Trial Networks; Request for Information and Comments

The Food and Drug Administration (FDA, the Agency, or we) is announcing the establishment of a docket to obtain information and comments from patients, patient advocates, the scientific community,...

federalregister.gov
Interesting read on how #orphandrug biotech @Pharnext plans to respond to #COVID19 by leveraging AI data forbes.com/sites/lawrencelig…
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