These are a few of the ongoing & new GIST clinical trials & programs currently enrolling. If you have questions or need help navigating a #ClinicalTrial, contact: Simran, ssingh@liferaftgroup.org #KQB198 #PEMIGIST #Pemigatinib #StrateGIST3 #ExpandedAccessProgram #Bezuclastinib

Really……..kinda wish it was…….. The only takeaway is that this patient suffers from #USH2A gene mutation 🧬 Under #FDA #ExpandedAccessProgram this is/will validate the scientific clinical gene-agnostic hypothesis for treating #RetinitisPigmentosa #OCU400 $OCGN

#OCU400 EAP - should not deter, inhibit, or preclude #Ocugen from treating patients, it should ensure they #TreatEveryone Given that some patients were not followed up following initial trials & EAP communications. #RightToTry #CompassionateUse #ExpandedAccessProgram $OCGN

aTyr announces #ExpandedAccessProgram for #efzofitimod for #pulmonarysarcoidosis. Individual Patient EAP intends to allow access for patients who complete Phase 3 EFZO-FIT™ study & wish to receive treatment with efzofitimod outside of the clinical trial. bit.ly/42LUpSU

#ouralscommunity took a tough blow today but let it be known that today also starts my year with #Pridopidine on #expandedaccessprogram “Expanded access is a pathway for a patient with an immediately life-threatening condition to gain access to an investigational medical

OncoSec is committed to delivering safer and more effective #cancer treatments that can provide long-term benefits for patients. Learn more about our #ExpandedAccessProgram here: bit.ly/3jbGLE6

#CompassionateUse is the marriage of the humanity of Right to Try & the science of the #FDA. The #ACTforALS empowers the FDA's existing #ExpandedAccessProgram to get #DrugsinBodies while increasing data for researchers Without it, people w #ALS are #DyingWaiting #ALSAwareness

We've initiated a rolling NDA submission for maralixibat for cholestsatic pruritus assoc. with #ALGS, & launched our #expandedaccessprogram. We're striving to make a meaningful impact on the lives of ALGS patients & families & today is a big step forward! bit.ly/32HZJIo

UPDATE-Gilead #ExpandedAccessProgram for #remdesivir site selection for #COVID19 pts in progress. Pearls 1)email COVID_Expanded_Access_HCP@gilead.com 2)sites will be selected based if surge, poor remdesivir #RCT access, regional reach & regulatory compliance. Stay tuned

Yes, but don't forget all, u MAY be able to "burn your 1 remdesivir IRB card" for ur 1st #expandedaccessprogram #remdesivir as u wait for IRB approval. This means, call IRB fill out Gilead form, get drug, hope drug is better than Ebola days. Send apology/flowers to IRB protocol

BREAKING NEWS: $GILD #Remdesivir the antiviral treatment against #coronavirus is transitioning to the #ExpandedAccessProgram to accelerate access to the treatment. It has proven effective through Compassionate use, currently in Phase 3 Clinical Trials #GILD #COVID19 #treatment

Thanks. Overall think the move to #remdesivir #expandedaccessprogram for #COVID19 pts is a GOOD thing - will be easier to get & criteria more transparent. However, immediate delay as 1)local #IRB application needs to be written, 2)IRB committee has to meet & approve->delay

Will provide more guidance in a few hours for #ExpandedAccessProgram process. But this will introduce delay for any sites/#COVID19 pts who can't get #RCT #remdesivir as local IRB committee has to approve application first

BREAKING NEWS-#Remdesivir #Gilead #CompassionatUseProgram for most critically ill #COVID19 patients SUSPENDED (preg women/kids OK). Changed to #ExpandedAccessProgram. Implications? 1)Individual need #IRB (inclusion/exclusion/consent) 2)sites should act NOW to prepare. Stay tuned

We have launched a new version of our #ExpandedAccessProgram and #ClinicalTrials Search #App. Download it for free at bit.ly/myT_app