Pediatric hematology/oncology | Stem cell biology | AML | Gene therapy | CRISPR
Joined December 2021
- Tweets 217
- Following 192
- Followers 325
- Likes 342
25 Photos and videos
Pinned Tweet
11 Nov 2024
Gene therapy is transforming how we treat genetic disorders, but what if mutations in more than 30 genes can cause similar symptoms?
Now published in @CellStemCell (cell.com/cell-stem-cell/full…), we report the development of a universal gene therapy for Diamond Blackfan anemia.
1/n
8
22
82
8,080
Apr 22
Congrats Walter! Trainees and folks looking for a new and exciting challenge: don’t pass up this opportunity to work with Walter!
Thrilled to share that I’ll be starting my lab as an Assistant Professor and Endowed Scholar in @UTSWMedCenter Molecular Biology Dept this Fall! 🥳 We’ll study #peroxisomes #mitochondria #metabolism via the lens of neonatology👶🏻, a very exciting frontier in medicine! #neotwitter
1
165
Richard Voit retweeted
Mar 30
❓A one-time, durable, and even reversible way to prevent thrombosis? In this preprint, led by @lrbzldz, we show that epigenome editing of 🩸 #StemCells can durably reprogram platelet function: biorxiv.org/content/10.64898…
6
42
143
19,122
Richard Voit retweeted
Mar 27
FDA just approved Kresladi (marnetegragene autotemcel) for severe LAD-I — a disease so rare there are ~25 new cases a year in the U.S. The pivotal data: 9 patients. 100% overall survival. All endpoints met. This approval is a masterclass in how to think about evidence standards when mechanism is unambiguous. fda.gov/news-events/press-an…
4
11
36
5,491
Richard Voit retweeted
Mar 27
In this piece, my mentor Stu Orkin and I (1) marvel at prime editing—discovery to disease correction for 2 patients after just 6 yr—wow Liu, Anzalone, Gori, Malech et al! & (2) consider the challenges to deliver genetic medicine’s promise for 2^n patients nejm.org/doi/full/10.1056/NE…
14
50
6,021
Richard Voit retweeted
We fund researchers like @kennethschen, one of the brilliant minds that is helping to shape the future of cancer research. V Foundation researchers, throughout their careers, have generated $22 billion in additional cancer research funding. We truly fund the best of the best.
2
8
725
Richard Voit retweeted
24 Dec 2025
MECOM promotes malignant stem cell–like states in aggressive AMLs by directly repressing prodifferentiation gene regulatory programs. Read the plenary paper in Blood: ow.ly/Nrko50XNqJk #BloodJournal #PlenaryPaper #AML
12
39
3,318
19 Dec 2025
Proud of you @tjflemin for your incredibly hard work on this. Now the next frontier: inhibiting this pathway in a clinically tractable way.
18 Dec 2025
Terrific to have our paper, led by @tjflemin, featured as a plenary article in @BloodPortfolio today: ashpublications.org/blood/ar…
3
562
15 Oct 2025
Congratulations @Mendell_lab. What an interesting mechanism!
14 Oct 2025
Colliding ribosomes are potent signals of cellular stress. But do cells use ‘programmed’ ribosome collisions to regulate gene expression? I’m excited to present a new story led by Frederick Rehfeld revealing that the answer is YES! Read on to find out how. biorxiv.org/content/10.1101/…
1
483
Richard Voit retweeted
Congrats! 👏👏👏 Two CRI scientists named 2025 Pew-Stewart & Pew Scholars — @JaviGBermudez & @HijaiShin — to advance cancer, biomedical research. Read more about their #relentlessdiscovery ⬇️ cri.utsw.edu/two-childrens-r… @pewtrusts
2
11
52
10,765
1 Aug 2025
Looking forward to the #NFRF2025 @UTSWScience in October. utsouthwestern.edu/education…. If you are an undifferentiated trainee @UTSWMedCenter, come check out highlights from new labs on campus.
1 Aug 2025
Committed to advancing treatments for children with blood disorders, @RichardVoit is exploring the complexities of hematopoietic stem cells to enhance targeted leukemia therapies. Discover more: voitlab.org/ #NFRF2025 #NFRF
2
10
677
Richard Voit retweeted
8 Jul 2025
Inspiring piece in @NatureCancer, "An unexpected career in cancer metabolism," highlights Dr. Ralph DeBerardinis & the pivotal moments that prompted him to pursue a career in cancer metabolism. @CRI_UTSW @HHMINEWS nature.com/articles/s43018-0…
1
11
58
4,795
Richard Voit retweeted
23 Jun 2025
Catalytic inhibition of KAT6/KAT7 enhances the efficacy and overcomes primary and acquired resistance to Menin inhibitors in MLL leukaemia - by
@ShellainaGordon @florian_perner, @Armstrong_dfci, @MAF_Dawson @TheDawsonLab
et al. doi.org/10.1158/2159-8290.CD… @PeterMacRes @DanaFarber
2
4
12
5,741
Richard Voit retweeted
23 Jun 2025
KAT6A and KAT7 Histone Acetyltransferase Complexes Are Molecular Dependencies and Therapeutic Targets in NUP98-Rearranged Acute Myeloid Leukemia
@NMichmerhuizen, Emily Heikamp, @Armstrong_dfci, @CMullighan and colleagues doi.org/10.1158/2159-8290.CD…
@StJudeResearch @DanaFarber
3
7
999
Richard Voit retweeted
22 Jun 2025
Be part of the Wagenblast Lab! We are hiring a Lab Manager for leukemia & blood stem cell research at @IcahnMountSinai in NYC, starting July 2025. See ad to apply!
9
21
2,823
4 Jun 2025
Congratulations @michaelpoeschla and @bloodgenes. Incredible work!
4 Jun 2025
Delighted to have our work on Polygenic Modifiers of #TelomereBiologyDisorders, led by @michaelpoeschla, along with @SashaGusevPosts, @mitchiela, @SharonSavageMD, @hemanth_tummala, and others, published as an advanced online paper in @jclinicalinvest today: jci.org/articles/view/191107
1
2
349
Richard Voit retweeted
22 May 2025
Excited to share with all our latest work on the use of single cell tools in following IDH mutant AML patients during their treatment! Out today @CellStemCell !! An amazing collaboration with @AkEisfeld & @PapaemmanuilLab & @landau_lab !!! Driven by the impressive @MariaSirenko and @soobeomlee & Zhengxi Sun at @NYUGSOM_Path
14
57
241
34,390
13 May 2025
We at voitlab.org are grateful to @TexasCCF for supporting our work. Thank you also to @dallascowboys @dak, @Jalen8Tolbert, @tonyromo, @TroyAikman for using their platform to raise awareness and funds for pediatric cancer research. youtu.be/KZwX8Mf7n5I
1
4
10
1,000
13 May 2025
Kids like KK motivate everything we do in the lab @utswcancer @CRI_UTSW @UTSW_PedsHemOnc. We are now hiring so if you are looking for the next step in your scientific journey or want to learn more about what we do, please reach out.
3
637
8 Apr 2025
Congratulations Elvin and team. This is a really elegant way to probe an important clinical question underlying aggressive AMLs.
8 Apr 2025
Thrilled to share the first pre-print from our lab! We tackled a big question: Why are some pediatric leukemias extremely aggressive? We explored the developmental origins of fusion-driven acute myeloid leukemia (AML). Let's dive in! #AML #NUP98 n/13
1
8
533
Richard Voit retweeted
3 Apr 2025
Delighted to have our Perturb-multiome paper, led by @jmartinrufino and #AlexisCaulier from our lab, published today in @ScienceMagazine. Please check out this powerful approach to decipher gene regulatory networks enriched for genetic variation: science.org/doi/10.1126/scie…
17
85
358
33,384